Alpha-1 antitrypsin (AAT) deficiency is a genetic disease where your body doesn’t make enough normal functioning AAT. AAT is a protein your liver makes. AAT has many important roles in your body, ...
Single Dose of BEAM-302 Led to Durable, Dose-dependent Increases in Total and Functional Alpha-1 Antitrypsin (AAT), Production of Corrected M-AAT, and Decreases in Mutant Z-AAT in Circulation Across ...
Researchers examined the medical costs for patients with a rare subset of chronic obstructive pulmonary disease (COPD) caused by a deficiency in alpha-1 antitrypsin receiving augmentation therapy.
BEAM-302 demonstrated safety and efficacy in increasing AAT levels and reducing mutant protein in alpha-1 antitrypsin deficiency patients. Beam Therapeutics announced promising initial results from ...
Sanofi’s efdoralprin alfa met all primary and key secondary endpoints in alpha-1 antitrypsin deficiency emphysema phase 2 studyEfdoralprin alfa ...
When a disease runs in your family, you don’t learn about it from textbooks. You learn about it at funerals, in hospital beds, and emergency rooms. My family has lost multiple members to Alpha-1 ...
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